Design, Characterization, and Lead Selection of Therapeutic miRNAs Targeting Huntingtin for Development of Gene Therapy for Huntington's Disease
- Jana Miniarikova
- , Ilaria Zanella
- , Angelina Huseinovic
- , Tom van der Zon
- , Evelyn Hanemaaijer
- , Raygene Martier
- , Annemart Koornneef
- , Amber L. Southwell
- , Michael R. Hayden
- , Sander J. van Deventer
- , Harald Petry
- , Pavlina Konstantinova
Research output: Contribution to journal › Article › peer-review
118
Citations
(Scopus)