TY - JOUR
T1 - Local application of otoprotective compounds other than sodium thiosulfate to prevent cisplatin-induced hearing loss
T2 - a systematic review
AU - Masroor, Amirhossein
AU - Streefkerk, Nienke
AU - Van Grotel, Martine
AU - Geller, James I.
AU - Ansari, Marc
AU - Bouffet, Eric
AU - Bleyer, Archie
AU - Fresneau, Brice
AU - Sullivan, Michael
AU - Knight, Kristin
AU - Kogner, Per
AU - Maibach, Rudolf
AU - O'neill, Allison F.
AU - Papadakis, Vassilios
AU - Rajput, Kaukab M.
AU - Brock, Penelope R.
AU - Veal, Gareth J.
AU - Hoetink, Alexander E.
AU - Huitema, Alwin D.R.
AU - Van Den Heuvel- Eibrink, Marry M.
N1 - Publisher Copyright:
© 2026 The Author(s). Published by Informa UK Limited, trading as Taylor & Francis Group.
PY - 2026
Y1 - 2026
N2 - Cisplatin-induced hearing loss (CIHL) in pediatric cancer patients is an irreversible and highly prevalent adverse effect with a devastating impact on quality of life. Sodium thiosulfate (STS) has recently been approved for systemic administration as an otoprotective agent in children. However, implementation of systemic STS has its challenges, and there is currently limited evidence to support local STS for children. This review investigates the potential value of locally administered otoprotective agents other than STS with a focus on future pediatric implementation. We conducted a systematic review on the efficacy and safety of locally applied non-STS otoprotective agents in in vivo settings. This included a summary of investigated drug delivery methods and administration routes. We identified 70 preclinical and eight clinical studies. Agents were categorized based on their biological mechanisms: anti-inflammatory, chemical deactivators, calcium blockers, biologicals, and miscellaneous mechanisms. Preclinical studies investigated 45 different agents. Dexamethasone and N-acetylcysteine were identified as efficacious agents recurrently and progressed to clinical trials. Dexamethasone was investigated in three randomized clinical trials (RCTs) and three non-randomized clinical studies and showed statistically significant but not clinically relevant benefit in two trials. N-acetylcysteine was investigated in two clinical trials and one RCT and was minimally effective in the RCT and in one clinical study. Our review did not identify available studies of local alternative otoprotective agents that could reliably replace systemic STS in terms of safety and efficacy for pediatric patients. Further research on the optimal dosage, delivery method, and timing of otoprotective agents is needed.
AB - Cisplatin-induced hearing loss (CIHL) in pediatric cancer patients is an irreversible and highly prevalent adverse effect with a devastating impact on quality of life. Sodium thiosulfate (STS) has recently been approved for systemic administration as an otoprotective agent in children. However, implementation of systemic STS has its challenges, and there is currently limited evidence to support local STS for children. This review investigates the potential value of locally administered otoprotective agents other than STS with a focus on future pediatric implementation. We conducted a systematic review on the efficacy and safety of locally applied non-STS otoprotective agents in in vivo settings. This included a summary of investigated drug delivery methods and administration routes. We identified 70 preclinical and eight clinical studies. Agents were categorized based on their biological mechanisms: anti-inflammatory, chemical deactivators, calcium blockers, biologicals, and miscellaneous mechanisms. Preclinical studies investigated 45 different agents. Dexamethasone and N-acetylcysteine were identified as efficacious agents recurrently and progressed to clinical trials. Dexamethasone was investigated in three randomized clinical trials (RCTs) and three non-randomized clinical studies and showed statistically significant but not clinically relevant benefit in two trials. N-acetylcysteine was investigated in two clinical trials and one RCT and was minimally effective in the RCT and in one clinical study. Our review did not identify available studies of local alternative otoprotective agents that could reliably replace systemic STS in terms of safety and efficacy for pediatric patients. Further research on the optimal dosage, delivery method, and timing of otoprotective agents is needed.
KW - Childhood cancer
KW - cisplatin
KW - hearing loss
KW - local intratympanic otoprotection
KW - ototoxicity
KW - Cisplatin/adverse effects
KW - Humans
KW - Hearing Loss/chemically induced
KW - Animals
KW - Protective Agents/administration & dosage
KW - Thiosulfates/administration & dosage
KW - Antineoplastic Agents/adverse effects
KW - Child
UR - https://www.scopus.com/pages/publications/105037773267
UR - https://www.tandfonline.com/doi/full/10.1080/10717544.2026.2665892
UR - https://www.mendeley.com/catalogue/f589de28-3d41-3213-852f-c583ff2c80b2/
U2 - 10.1080/10717544.2026.2665892
DO - 10.1080/10717544.2026.2665892
M3 - Review article
C2 - 42068011
AN - SCOPUS:105037773267
SN - 1521-0464
VL - 33
JO - Drug delivery
JF - Drug delivery
IS - 1
M1 - 2665892
ER -